BONAPH1DE, A Prospective Observational Study of Patients With Primary Hyperoxaluria Type 1 (PH1)
Primary Hyperoxaluria Type 1The purpose of this study is to describe the natural history and progression of patients diagnosed with PH1, and to characterize the long-term real-world safety and effectiveness of lumasiran.
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Participation Requirements
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Sex:
ALL -
Eligible Ages:
0 and up
Participation Criteria
Inclusion Criteria:
* Documented diagnosis of PH1, per physician's determination
Exclusion Criteria:
* Currently enrolled in a clinical trial for any investigational agent
Study Location
Clinical Trial Site
Clinical Trial SiteToronto, Ontario
Canada
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Clinical Trial Site
Clinical Trial SiteHamilton, Ontario
Canada
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Clinical Trial Site
Clinical Trial SiteLaurier, Quebec
Canada
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- Study Sponsored By
- Alnylam Pharmaceuticals
- Participants Required
- More Information
- Study ID:
NCT04982393